기술동향
A Decade of Innovation in Rare Diseases
- 등록일2015-03-10
- 조회수4492
- 분류기술동향 > 레드바이오 > 의약기술
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자료발간일
2015-02-24
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출처
PhRMA
- 원문링크
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키워드
#Rare Diseases#A Decade of Innovation#Orphan Drug Act#희귀질환#Leukemia
- 첨부파일
PhRMA-Decade-of-Innovation-Rare-Diseases.pdf
[Introduction]
● The Orphan Drug Act: Crucial Incentives for Continued Advances against Rare Diseases
● Chronic Myelogenous Leukemia: Scientific Advances Propel New Treatment Options for Patients
Spotlight: Neonatal-Onset Multisystem Inflammatory Disease
● Chronic Lymphocytic Leukemia: New Era of Targeted Therapies
Spotlight: Mucopolysaccharidosis Type IVA
● Pulmonary Arterial Hypertension: Slowing Progression and Keeping Patients Active
Spotlight: Homozygous Familial Hypercholesterolemia
● Hereditary Angioedema: Putting Disease Management in the Hands of Patients
Spotlight: Huntington’s Disease
● Cystic Fibrosis: Attacking the Symptoms and the Cause Spotlight: Gaucher Disease
Continued Progress for Patients with Rare Diseases
...................(계속)
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